PPMD - Duchenne app now downloading

Parent Project Muscular Dystrophy: Home: "Download PPMD’s New Duchenne App
PPMD is excited to announce the release of our new, free mobile applications designed specifically for the iPhone, iPad, and Androids. PPMD's new app will put emergency care information, critical research news, and advocacy alerts at your fingertips, instantaneously"

Results of Prosensa’s Extended Phase I/II Exon-skipping Trial in Duchenne Muscular Dystrophy Published in the New England Journal of Medicine - Prosensa

Results of Prosensa’s Extended Phase I/II Exon-skipping Trial in Duchenne Muscular Dystrophy Published in the New England Journal of Medicine - Prosensa: "Prosensa,, announces the publication of results from a phase I/II and 12-week extension study of its lead product, PRO051 (GSK2402968) for the treatment of Duchenne Muscular Dystrophy (DMD) in the New England Journal of Medicine (NEJM)[1]."

Parent Project Muscular Dystrophy: Mobile App

Parent Project Muscular Dystrophy: Mobile App: "The next time you are meeting with your doctor and want to access information from PPMD's vast research or care archive, you can. The next time you have to take your child to the emergency room and are unsure what safety measures must be taken into consideration, the PPMD app is there. The next time you are in an IEP meeting and need to make sure you went through your checklist of discussion items, your go-to resource is available"

Transparent fish to make human biology clearer

Transparent fish to make human biology clearer: "Zebrafish are genetically similar to humans and are good models for human biology and disease. Now, researchers at Children's Hospital Boston have created a zebrafish that is transparent throughout its life. The new fish allows scientists to directly view its internal organs, and observe processes like tumor metastasis and blood production after bone-marrow transplant in a living organism."

New insight into Duchenne muscular dystrophy

New insight into Duchenne muscular dystrophy: "Armed with a zebrafish model of Duchenne muscular dystrophy (DMD) and a library of 1,200 chemicals already approved for human use, researchers at Children's Hospital Boston have identified a compound that reverses the loss of muscle structure and function associated with DMD, seemingly by compensating for the loss of a critical protein."

2012 Walt Disney World Marathon Weekend Registration is Open!

Parent Project Muscular Dystrophy:: "2012 Walt Disney World Marathon Weekend Registration is Open!
Register today for a magical family weekend."

GSK Now Recruiting for Exon 51 Clinical Trial in Non-Ambulatory Boys

Parent Project Muscular Dystrophy: Home: "GSK Now Recruiting for Exon 51 Clinical Trial in Non-Ambulatory Boys
This study will assess the pharmacokinetics, safety, and tolerability of GSK2402968 after a single administration, at escalating dose levels, in non-ambulatory boys with Duchenne who have a dystrophin gene mutation amenable to an exon 51 skip."