Thursday, 11 December 2014

» Sarepta Thereaputics release information on trial for SRP-4053 for skipping exon 53 Action Duchenne

» Sarepta Thereaputics release information on trial for SRP-4053 for skipping exon 53 Action Duchenne: "Sarepta Therapeutics have released information regarding the clinical trial for their drug candidate SRP-4053 for skipping exon 53, which is taking place in Europe.

Enrolment for the London centre at Great Ormond Street Hospital is currently taking place, with the Newcastle Centre planned for the future.
 
Eligibility criteria and other information is included in the posting on the clinical trials website.

 

Inclusion criteria includes:

 

being amenable to exon 53 skipping,
stable pulmonary and cardiac function,
minimum performance on 6 minute walk test, North Star Ambulatory Assessment, and rise (Gowers) test as specified in the study protocol,
On a stable dose of corticosteroids for at least 6 months.
Aged between 6-15 years old
Intact right and left biceps muscles or an alternative upper arm muscle group."



'via Blog this'

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