Tuesday 20 December 2011

Parent Project Muscular Dystrophy: Leading the fight to end Duchenne

Parent Project Muscular Dystrophy: Leading the fight to end Duchenne: "PPMD is happy to be supporting Summit PLC with its utrophin upregulation drug candidate SMT C1100. The funding provided will enable Summit to manufacture a new formulation of SMT C1100 and conduct a Phase I clinical trial in healthy volunteers."

'via Blog this'

Thursday 15 December 2011

Help Santa deliver his toys and support Action Duchenne with new Christmassy iPhone & iPad App from Rantmedia - View News Article - Action Duchenne - Fighting for a cure for muscular dystrophy

Help Santa deliver his toys and support Action Duchenne with new Christmassy iPhone & iPad App from Rantmedia - View News Article - Action Duchenne - Fighting for a cure for muscular dystrophy: "Download Santa’s Sleigh Ride, enjoy the fun and 15% of proceeds go to Action Duchenne from http://itunes.apple.com/gb/app/santas-sleigh-ride/id477668167

ARTICLE POSTED: 15 DECEMBER 2011 PERMANENT LINK
RantMedia has designed a fabulous new iPhone & iPad app called Santa’s Sleigh Ride where you get Santa and his reindeer to jump over toys, decorations and other festive things. The game is easy to play, yet highly addictive with increasingly fast and furious levels. "

'via Blog this'

Tuesday 6 December 2011

World Muscle Society 2011 Report - PPMD Community

World Muscle Society 2011 Report - PPMD Community: "At the recent World Muscle Society meeting, which took place in Portugal, a great deal of new data on exon skipping was presented, both on the status of current human clinical trials and on the efforts of investigators to improve the efficiency of the technique by combining exon-skipping with gene and stem cell delivery. Below are a few highlights from the meeting with the caveat that it was impossible to cover every poster and talk. "

'via Blog this'

Thursday 1 December 2011

New gene therapy approach safe for patients with muscular dystrophy

New gene therapy approach safe for patients with muscular dystrophy: "Researchers at the University of North Carolina at Chapel Hill have shown that it is safe to cut and paste together different viruses in an effort to create the ultimate vehicle for gene therapy. In a phase I clinical trial, the investigators found no side effects from using a "chimeric" virus to deliver replacement genes for an essential muscle protein in patients with muscular dystrophy."

'via Blog this'