Parent Project Muscular Dystrophy: Leading the fight to end Duchenne

Parent Project Muscular Dystrophy: Leading the fight to end Duchenne: "PPMD is happy to be supporting Summit PLC with its utrophin upregulation drug candidate SMT C1100. The funding provided will enable Summit to manufacture a new formulation of SMT C1100 and conduct a Phase I clinical trial in healthy volunteers."

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Help Santa deliver his toys and support Action Duchenne with new Christmassy iPhone & iPad App from Rantmedia - View News Article - Action Duchenne - Fighting for a cure for muscular dystrophy

Help Santa deliver his toys and support Action Duchenne with new Christmassy iPhone & iPad App from Rantmedia - View News Article - Action Duchenne - Fighting for a cure for muscular dystrophy: "Download Santa’s Sleigh Ride, enjoy the fun and 15% of proceeds go to Action Duchenne from http://itunes.apple.com/gb/app/santas-sleigh-ride/id477668167

ARTICLE POSTED: 15 DECEMBER 2011 PERMANENT LINK
RantMedia has designed a fabulous new iPhone & iPad app called Santa’s Sleigh Ride where you get Santa and his reindeer to jump over toys, decorations and other festive things. The game is easy to play, yet highly addictive with increasingly fast and furious levels. "

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World Muscle Society 2011 Report - PPMD Community

World Muscle Society 2011 Report - PPMD Community: "At the recent World Muscle Society meeting, which took place in Portugal, a great deal of new data on exon skipping was presented, both on the status of current human clinical trials and on the efforts of investigators to improve the efficiency of the technique by combining exon-skipping with gene and stem cell delivery. Below are a few highlights from the meeting with the caveat that it was impossible to cover every poster and talk. "

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New gene therapy approach safe for patients with muscular dystrophy

New gene therapy approach safe for patients with muscular dystrophy: "Researchers at the University of North Carolina at Chapel Hill have shown that it is safe to cut and paste together different viruses in an effort to create the ultimate vehicle for gene therapy. In a phase I clinical trial, the investigators found no side effects from using a "chimeric" virus to deliver replacement genes for an essential muscle protein in patients with muscular dystrophy."

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Medicine thrown into crisis by stem cell ruling - Science, News - The Independent

Medicine thrown into crisis by stem cell ruling - Science, News - The Independent: "British medical researchers have condemned a Europe-wide ban on the patenting of stem cell inventions derived from human embryos – setting back possible new treatments for a range of disorders, from heart disease and diabetes to blindness and Parkinson's."

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AVI BioPharma - News Release

AVI BioPharma - News Release: "AVI BioPharma, Inc. (NASDAQ: AVII), a developer of RNA-based therapeutics, today announced data presentations for eteplirsen (the non-proprietary name assigned to AVI-4658), the Company's investigational exon skipping therapy for the treatment of Duchenne muscular dystrophy, at the 16th International Congress of the World Muscle Society taking place Oct. 18-22, 2011 in Almancil, Algarve, Portugal."

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Study in Need of Boys with Duchenne: MRI and Biomarkers for DMD (ImagingDMD)

Study in Need of Boys with Duchenne: MRI and Biomarkers for DMD (ImagingDMD): "This study focuses on developing Magnetic Resonance Imaging (MRI) as a tool to monitor disease progression in Duchenne and to serve as an outcome measure for clinical trials. The aim of the study is to determine whether noninvasive MRI outcome measures can replace muscle biopsies in evaluating the effectiveness of new treatments in future clinical trials. A second goal of this study is to characterize the progressive involvement of the lower extremity muscles to help guide the design of future clinical trials. This study is funded by the NIH – NIAMS/NINDS. "

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