PPMD Leads Critical Letter for Rare Disease Community - PPMD Community

PPMD Leads Critical Letter for Rare Disease Community - PPMD Community: Parent Project Muscular Dystrophy (PPMD) has teamed up with�EveryLife Foundation for Rare Diseases�and�Genetic Alliance�to galvanize the rare disease community and send a strong message to Congress to ensure the most important provisions for the rare disease community were included in the final�Prescription Drug User Fee Act (PDUFA) legislation. The provisions are aimed at accelerating Food and Drug Administration (FDA) review of therapies to treat rare diseases and to enable FDA to more aggressively engage external experts in reviewing candidate therapies.